The discovery of therapeutic nucleic acids represents one of the major breakthroughs of the genomic revolution, since they are capable of controlling specific protein expression in cells at the source of the pathogenesis. Many genetic degenerative diseases are difficult or impossible to cure because we lack medications capable of reprogramming gene expression in cells. In order to address this important gap, Prof. Matthew Wood focuses on novel gene therapies for the treatment of neuromuscular degenerative disorders.